ROCHESTER, N.Y. – Researchers at Golisano Children’s Hospital have received a multi-million-dollar grant to lead a ...

Recent headlines in the U.K. lauded the approval of a new sickle cell cure using gene-editing technology. Columnist Mary ...

There are several treatments ... sickle cell anemia in Québec. It helps improve the quality of life of families living with the disease by providing various services, such as family respite and ...

Thanks to the Give Miami Day fundraiser, Beyond Grey can offer over 180 free therapy sessions to students in need. Eligible students—ages 18 to 27 with no access to mental health care—can ...

A 64-year-old woman is dead after she was hit by a driver in a truck while she stood on the sidewalk. The tragic scene happened Saturday night in South Philadelphia. Officials say the driver of ...

Gene therapy emerges as ... Research continues pushing treatment possibilities beyond current limitations. Medical teams explore novel approaches to cell regeneration and vision protection.

Toddlers who were born with the most severe form of childhood blindness can now see after groundbreaking gene therapy treatment at an NHS hospital. The children, who suffer from an extremely rare ...

Electroretinograms, however, are usually not detectable in Leber congenital amaurosis, and signals from a small region treated with gene therapy might be lost in noise. For this study, 7 investigators ...

Pfizer is pulling further away from the gene therapy field with its decision ... the company decided to stop distributing the sickle cell disease treatment Oxbryta after a phase 3 trial turned ...

Jace, 6, was born with a rare and aggressive eye condition An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood blindness - gain ...

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood blindness - gain "life-changing improvements" to their sight, according to ...