ROCHESTER, N.Y. – Researchers at Golisano Children’s Hospital have received a multi-million-dollar grant to lead a ...

Recent headlines in the U.K. lauded the approval of a new sickle cell cure using gene-editing technology. Columnist Mary ...

Gene therapy emerges as ... Research continues pushing treatment possibilities beyond current limitations. Medical teams explore novel approaches to cell regeneration and vision protection.

Toddlers who were born with the most severe form of childhood blindness can now see after groundbreaking gene therapy treatment at an NHS hospital. The children, who suffer from an extremely rare ...

Standard treatment of small-cell lung cancer involves combination chemotherapy with a regimen that includes cisplatin. Treatment cycles are typically repeated every 3 weeks. People receive ...

Pfizer is pulling further away from the gene therapy field with its decision ... the company decided to stop distributing the sickle cell disease treatment Oxbryta after a phase 3 trial turned ...

Jace, 6, was born with a rare and aggressive eye condition An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood blindness - gain ...

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood blindness - gain "life-changing improvements" to their sight, according to ...

CHOP doctors Alexis Thompson and Stephan Grupp are named "Disruptors of the Year" in the second annual Philadelphia Citizen of the Year Awards. Dr. Thompson and Dr. Grupp are recognized for being ...

(CRISPR-Cas9), to treat β-thalassemia and sickle cell disease. 8 Advent and advancements in gene editing tools and cell therapy approaches, including autologous chimeric antigen receptor (CAR ...

The new lentiviral vector-based gene therapy works by inserting a functioning ... by inserting their genetic material into their host cell's genome. By modifying lentiviruses, scientists have ...