The research shows that as long as essential genes remain intact, our genomes can tolerate significant structural changes, ...

Australian cancer researchers are the first to establish a next-generation gene-editing tool for modeling and interrogating human disease.

Complementary discoveries have the potential to enhance treatment options for antibiotic-resistant infections. Researchers at ...

The most complex engineering of human cell lines ever has been achieved by scientists, revealing that our genomes are more resilient to significant structural changes than was previously thought.

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

CRISPR, short for Clustered Regularly Interspaced Short Palindromic Repeats, is a groundbreaking gene-editing technology that ...

Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell disease (SCD) patients to access the CRISPR/Cas9 gene-edited therapy, CASGEVY® ...

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

Australian researchers have successfully introduced an improved version of Cas12a gene-editing enzyme in mice.

January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...