‘Much-needed hope’ as CRISPR gene editing therapy recommended for sickle cell disease
Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
Sickle cell disease ‘cure’ to be offered to NHS patients
Around 1,700 people could be eligible for the one-time treatment, which is seen as a less risky alternative to a donor stem ...
Sickle cell patients share delight over approval of new treatment
A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle cell disease. Casgevy, also ...
Science Media Centre2d
expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease
January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...
EurekAlert!3d
No scientific link found between sickle cell trait and sudden death
A systematic literature review found no evidence to support that physical exertion without rhabdomyolysis (muscle breakdown) or heat injury can cause sudden death for individuals with sickle cell ...
Daily Monitor5d
Preventing sickle cell disease through modern science
Abnormal cells can clog blood vessels, leading to severe pain episodes and restricting oxygen delivery to vital organs ...
Medindia11d
Rigel's Fostamatinib Being Studied by National Institute of Health in Patients with Sickle Cell Disease
First patient enrolled in NIH/NHLBI-sponsored Phase 1 Study of fostamatinib, Rigel's oral SYK inhibitor "Our Phase 1 study evaluating fostamatinib in patients with sickle cell disease is an ...
Research identifies PICH protein as key player in preventing chromosome breakage linked to cancer
Researchers at The University of Hong Kong (HKU) have made an exciting discovery about how human cells protect DNA during ...
Medindia12d
YolTech Therapeutics to Initiate a Clinical Trial for YOLT-204, a First-in-Class Bone Marrow-Targeted In Vivo Gene Editing Therapy for ß-Thalassemia
YolTech Therapeutics, a clinical-stage gene editing company dedicated to delivering lifelong cures, announced the initiation of a clinical trial for YOLT-204 , an investigational ...
I’m 52 and get up twice in the night to pee, help! Dr Zoe reveals the health conditions behind ‘nocturia’
DEMENTIA will affect one in three of us in our lifetime. So it is no wonder that 54 per cent of Sun readers are worried about ...
thewhistler.ng12d
Why I Made First Class Despite Living With Sickle Cell — Unilag Graduate
She wrote most of her examinations on the hospital bed, yet she came out as one of the brightest graduates the University of ...
AOL16d
Pharma giant Regeneron is spending $119.5M on the world’s largest, most diverse genetic database using DNA from patient volunteers
“The world needed this to exist,” Myerson says. The Regeneron Genetics Center has pledged to sequence the exomes—the protein-coding parts of genomes—of the project’s first 10 million patient ...