People living with sickle cell are apprehensive about a revolutionary new one-off treatment that has just been approved for use on the NHS. | ITV News Granada ...

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

For Vertex these days, it’s all about the launches of three new products—sickle cell disease gene therapy Casgevy, the ...

The Food and Drug Administration approval in December 2023 of the first CRISPR therapeutic, Casgevy to treat sickle cell, came 11 years after the discovery of the revolutionary gene-editing technology ...

Casgevy, made by Boston-based Vertex Pharmaceuticals and Crispr Therapeutics in Switzerland, works by editing the faulty HBB gene behind both conditions in a patient's bone marrow stem cells so ...

The gene-editing treatment will be available to certain patients with sickle cell disease in England as Vertex commits to collecting additional data.

With the addition of Casgevy, Children’s Hospital Los Angeles now offers two gene therapies for sickle cell, the first being Lyfgenia.

However, he added: "We remain acutely aware that not everyone with sickle cell will be eligible for the potentially ...

Vertex Pharmaceuticals (VRTX) announced a reimbursement agreement with NHS England for eligible sickle cell disease patients to access the ...

The reimbursement agreement comes as the National Institute for Health and Care Excellence (NICE) issues positive guidance recommending CASGEVY ... industry's top places to work, including ...

Vertex Pharmaceuticals Inc. (VRTX), a commercial-stage global biotechnology company, announced Friday a reimbursement agreement with ...

However, he added: "We remain acutely aware that not everyone with sickle cell will be eligible for the potentially life-changing benefits of Casgevy. "There is still much work ahead to ensure ...