Research in genetics and biotechnology has advanced by leaps and bounds in recent years, offering new hope for the treatment ...

For nearly 20 years, Spuler and her collaborators have been working to understand dysferlin, its role in muscular dystrophy and ways to cure these ... Escobar uses CRISPR-Cas9, which is often ...

Researchers at the Experimental and Clinical Research Center in Berlin are developing a targeted treatment for muscular dystrophy with the help of gene ... To fix the dysferlin mutation, Escobar uses ...

"This type of gene editing should also allow for the treatment of diseases whose origin is not genetic or whose origin cannot ...

A patient would only need a single treatment. CRISPR-Cas9 is comprised of ... is pursuing treatments for cystic fibrosis. Duchenne Muscular Dystrophy (DMD), hemophilia A and B, HIV, inherited ...