VIJAYAWADA: Sickle cell anaemia and thalassemia remain major health concerns in the State, particularly among tribal ...
Charity organisation Sickle Cell Society has described the recommendation as a “major breakthrough” for sickle cell patients.
Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell ...
Accumulation of clots causes some of the most severe symptoms of sickle cell disease, including strokes, kidney failure, ...
According to research studies and demographic surveys by the Union Ministry of Tribal Affairs and genetic researchers, sickle cell disease is widespread in many tribal groups of India, especially amon ...
The therapy involves taking stem cells out of a patient's bone marrow and editing a gene in the cells in a laboratory and ...
London: Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease ... the NHS in August to treat beta thalassemia, another rare ...
Clinical trials for exa-cel have shown promising results that it has been authorised by the FDA and MHRA for use in beta thalassemia and sickle cell disease. These successes make CRISPR technology, as ...
The company has approved medicines that treat the underlying causes of multiple serious diseases and conditions — cystic fibrosis, sickle cell disease, transfusion-dependent beta thalassemia and ...
January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...
A gene-editing therapy for sickle cell ... living with sickle cell has access to the care, treatments, and support they ...
Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...