The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...
A "groundbreaking" £1.65 million treatment has been approved for use on the NHS, offering patients with severe sickle cell ...
Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell disease (SCD) patients to access the CRISPR/Cas9 gene-edited therapy, CASGEVY® ...
These sickle cells do not live as long as healthy red ... for the potentially life-changing benefits of Casgevy. "There is still much work ahead to ensure that everyone living with sickle cell ...
President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program ...
January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...
The Exa-cel gene therapy treatment is at the forefront of medical technology. It takes the person’s DNA and “edits” out the faulty sickle gene. It’s expensive, too. According to the manufacturer, ...