Gene editing is already being used to treat a handful of rare genetic diseases; however, most therapies involve breaking or ...

Mitochondrial diseases only happen when mutations overrun healthy DNA. Even a small amount of normal mitochondrial DNA can protect against mutations, suggesting gene editing could be a way to tackle ...

Accumulation of clots causes some of the most severe symptoms of sickle cell disease, including strokes, kidney failure, ...

Australian cancer researchers are the first to establish a next-generation gene-editing tool for modeling and interrogating human disease.

Researchers developed an epigenetic editing approach to silence the PCSK9 gene, achieving long-term cholesterol reduction ...

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

In a shift away from GMOS, aka genetically modified organisms, important research is continuing in gene editing, sometimes ...

Australian researchers have successfully introduced an improved version of Cas12a gene-editing enzyme in mice.

A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...

Attorneys general from 22 states filed a lawsuit Monday against the Trump administration for slashing funding for medical and ...

Gene therapies to treat rheumatoid arthritis have evolved slowly, but one is ready to move into human trials and an ...

A GROUNDBREAKING genetic treatment with the potential to cure sickle cell disease will be rolled out on the NHS. The one-off ...