Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
Around 1,700 people could be eligible for the one-time treatment, which is seen as a less risky alternative to a donor stem ...
January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...
Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...
A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...
The discovery of the CRISPR/Cas9 gene editing tool won two researchers, Emmanuelle Charpentier and Jennifer A. Doudna, the Nobel Prize in Chemistry in 2020. Exa-cel, also called Casgevy ...
The treatment uses gene-editing tool Crispr, which earned its inventors the Nobel Prize in chemistry in 2020. Casgevy, also known as exa-cel, was the first treatment to be licensed using gene ...
The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...
Casgevy, also known as exa-cel, was the first treatment to be licensed using gene-editing tool Crispr, which earned its ...
Casgevy, also known as exa-cel, was the first treatment to be licensed using gene-editing tool Crispr (Alamy/PA) A £1.65 million treatment has been approved for use for some NHS patients ...