Healio9d
Vanzacaftor, tezacaftor, deutivacaftor safe in children with cystic fibrosis
Patients aged 6 to 11 years with cystic fibrosis receiving 24-week once-daily vanzacaftor/tezacaftor/deutivacaftor generally ...
EurekAlert!1d
Lurie Children’s campaign urges parents to follow up right away if newborn screening results are abnormal
Ann & Robert H. Lurie Children’s Hospital of Chicago launched a newborn screening awareness campaign, with signage on public transit and billboards across Chicago urging parents to contact their child ...
imt.ie9d
Call for children with cystic fibrosis and rare genes to gain access to life-saving therapy
Some people with cystic fibrosis still do not have access to the life-changing modulator therapy drugs, despite wider EMA ...
Independent.ie6d
‘Time is precious’ – children with rare cystic fibrosis gene denied access to potentially life-extending therapies
Children whose cystic fibrosis is caused by a rare gene variant are excluded from a new treatment which could potentially ...