A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...
Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
A £1.65 million treatment has been approved for use for some NHS patients, offering hope of a cure to those with an inherited ...
NHS officials estimate that around 50 people a year will receive treatment now that it has been approved for use for certain ...
The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...
An Oxfordshire university student is among those set to receive a "transformative" gene-therapy treatment on the NHS for sickle ...
The human genome encodes potentially thousands of tiny proteins that were previously overlooked. The search is on to find out ...
A revolutionary gene therapy treatment costing a staggering £1.65 million has been approved for NHS use, offering patients ...
January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...
One sickle cell patient told ITV News the new gene therapy being rolled out for use on the NHS means they "finally have something to look towards". | ITV National News ...
Casgevy was the first drug to be licensed based on CRISPR, which earned its discoverers a Nobel Prize in 2020. The one-shot therapy is an ex vivo application of the technology, meaning that bone ...
The company will use the funding to advance clinical trials for Tune-401, the epigenetic silencing drug for treating chronic ...