Breakthrough treatments offer some sickle cell sufferers a cure, but barriers remain
Esther Nkemakolam runs her fingers through kinetic sand and sings a “Moana” song as UPMC Children’s Hospital nurse Taylor ...
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New sickle cell treatment cures disease at lower cost than gene therapies
A new type of bone marrow transplant can cure sickle cell disease with only half of the donor's cell proteins matching, ...
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Golisano Children’s Hospital receives multi-million dollar grant to lead first-of-its-kind study on sickle cell disease treatments
ROCHESTER, N.Y. – Researchers at Golisano Children’s Hospital have received a multi-million-dollar grant to lead a ...
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Sickle cell gene therapy Casgevy finally cleared for NHS use
Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease (SCD), Casgevy, has been given the green light for use by the NHS in England under a managed access ...