Want to stay on top of the science and politics driving biotech today? Sign up to get our biotech newsletter in your inbox. Good morning. I'm still ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

Considering taking supplements to treat beta thalassemia? Below is a list of common natural remedies used to treat or reduce the symptoms of beta thalassemia. Follow the links to read common uses ...

Non-transfusion-dependent thalassemia encompasses three clinically distinct forms -- beta-thalassaemia intermedia, hemoglobin E/beta-thalassaemia (mild and moderate forms), and al ...

You most likely have beta thalassemia minor (one normal gene and one that causes low beta-cell-chain production), which consists of mild anemia and very small cells. This condition can look very ...

An ad hoc committee of the National Academies of Sciences, Engineering, and Medicine will develop a strategic plan and blueprint for addressing thalassemia in the United States. In conducting its work ...

There were no serious adverse events or treatment-related mortalities. Evidence Rating Level: 2 (Good) Study Rundown: Transfusion-dependent β-thalassemia (TDT) is a condition that results in iron ...

By type, the beta thalassemia segment accounted for the highest revenue-grossing segment in the global thalassemia market in 2023 owing to the high prevalence and severity of the condition ...

Discover top medications for 'treating Thalassemia'? This page compiles essential information on generic and brand-name drugs specifically used for Thalassemia treatment.Here, you can explore ...

Beta-thalassemia is a rare blood disorder caused by a genetic defect in hemoglobin. Several manufacturers are developing novel treatments for the disease, including Vertex, which has partnered ...

for the treatment of adult patients with non-transfusion-dependent and transfusion-dependent alpha- or beta-thalassemia, has been accepted for review by the FDA. The supplemental New Drug ...