Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
Gene editing promised a revolution, but biotech layoffs, stock slumps, and industry struggles reveal a stark reality: CRISPR ...
Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.
Around 1,700 people could be eligible for the one-time treatment, which is seen as a less risky alternative to a donor stem ...
People in England with sickle cell will be able to get the world’s first CRISPR-based medicine under an agreement between the ...
A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle cell disease. Casgevy, also ...
People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...
A GROUNDBREAKING genetic treatment with the potential to cure sickle cell disease will be rolled out on the NHS. The one-off ...
Charity organisation Sickle Cell Society has described the recommendation as a “major breakthrough” for sickle cell patients.
This switches to the adult form once they are born. Crucially foetal haemoglobin is not affected by sickle cell disease, so ...
One sickle cell patient told ITV News the new gene therapy being rolled out for use on the NHS means they "finally have something to look towards". | ITV National News ...
Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...