New gene therapies could transform sickle cell treatment forever. A future without pain crises or hospitalizations may finally be within reach.

A groundbreaking sickle cell disease treatment has been approved for use in the UK's National Health Service (NHS). The treatment offers patients with severe forms of the condition hope for a ...

Our fundamental challenge is not simply to create the data. Rather, it is to collect and analyze it systematically. Doing so ...

Exagamglogene autotemcel (exa-cel) gene therapy offers a potential cure for severe sickle cell disease, now available on NHS.

A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...

Can we predict that natural selection will weed out genetic disease over time? Sickle-cell trait haplotype distribution shows the genetic advantages of this mutation. In the deoxygenated ...

A sickle cell disease “cure” is to be offered to NHS patients for the first time. The £1.65 million gene therapy called exa-cel, also known under the brand name Casgevy, uses a Nobel Prize ...

Would the transplant work? What would it look like to have a successful stem cell transplant? Would it be a cure for my sickle cell disease? It was a decision I could think about making because my ...

VA lawmakers are considering a proposed bill that could boost funding for research and care related to sickle cell disease, ...

A "groundbreaking" £1.65 million treatment has been approved for use on the NHS, offering patients with severe sickle cell disease some hope of a cure. It is believed around 1,700 people could be ...