for the treatment of cystic fibrosis in patients with at least one F508del mutation or another treatment-responsive mutation in the CFTR gene. The fixed-dose triple-combination therapy ...
Despite new medication, cystic fibrosis often leads to permanent lung damage. Working with an international team, researchers ...
By the time Enid Katz was two years old, she had already suffered through several bouts of bronchitis and was always hungry, ...
Allison John and Rocky When Allison John was 13 and watching the science programme Tomorrow’s World , a segment on gene therapy came up. This was cutting edge stuff in the early 1990s and John had ...
The Massachusetts-based biotech plans to use the funds to push its candidates into mid-stage clinical trials in a space ...
The biotech is evaluating several cystic fibrosis medicines that could either work alongside Vertex’s top-selling Trikafta or ...
Sionna Therapeutics is eyeing a $156 million IPO as the cystic-fibrosis-focused biotech looks to take its lead candidate into ...
A new EMA approval has expanded the use of Vertex Pharma’s cystic fibrosis therapy Symkevi to children as young as six if they have specific gene mutations. The regulator has given a green light ...
Irish Independent on MSN12d
Wicklow mother calls for access to life-saving therapy for son with rare form of Cystic FibrosisA Wicklow mother is among a concerned group of parents who are calling for individual trials of the modulator therapies for ...
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