Uta Griesenbach, Eric W.F.W. Alton, Department of Gene Therapy, Faculty of Medicine ... proof-of-principle for gene transfer into the cystic fibrosis (CF) lung. It is currently unknown whether ...

In their 2019 paper, Liu’s team used prime editing to alter the gene mutations ... of genetic therapy treatments for those with rarer CF mutations too,” said Lucy Allen, a lung biologist and research ...

It will also enhance ReCode's existing RCT2100 clinical programme, an investigational inhaled messenger ribonucleic acid (mRNA) therapy ... secure funds for cystic fibrosis gene correction ...

Vertex Pharmaceuticals (NASDAQ:VRTX), a global biotechnology company with a market capitalization of $119.1 billion known for its transformative cystic fibrosis (CF) treatments, finds itself at a ...

It is a genetic disorder that can pass to children when both biological parents carry the atypical gene relating to it. There is currently no cure for cystic fibrosis. However, doctors might use ...

Sophie would make a world record for being the first man or woman with cystic fibrosis to row across the Atlantic, while at ...

Some people with cystic fibrosis still do not have access to the life-changing modulator therapy drugs, despite wider EMA ...

Children whose cystic fibrosis is caused by a rare gene variant are excluded from a new treatment which could potentially slow the decline in their lung function, it has emerged. A group of ...

A new EMA approval has expanded the use of Vertex Pharma’s cystic fibrosis therapy Symkevi to children as young as six if they have specific gene mutations. The regulator has given a green light ...

Adoption of Triple Combination Therapy Accelerates at Unprecedented Rates as Precision Medicine Revolution ContinuesRockville, MD, Jan. 29, 2025 (GLOBE NEWSWIRE) -- According to Fact.MR, a market ...

A Wicklow mother is among a concerned group of parents who are calling for individual trials of the modulator therapies for ...