Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
Sickle cell patients share delight over approval of new treatment - Health officials have approved a £1.65 million treatment ...
People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...
With a rise in Trikafta demand, the investors have assigned a higher valuation multiple for VRTX stock. The increase in VRTX ...
One sickle cell patient told ITV News the new gene therapy being rolled out for use on the NHS means they "finally have something to look towards". | ITV National News ...
Despite securing approval for its first marketed ... It became the first gene-editing treatment that uses the Nobel Prize-winning CRISPR technique, an impressive achievement by CRISPR Therapeutics.
Vertex Pharmaceuticals Inc. (VRTX), a commercial-stage global biotechnology company, announced Friday a reimbursement agreement with ...
A cutting-edge gene therapy has been approved for NHS use for ... was the first treatment to be licensed using gene-editing tool Crispr, which earned its inventors the Nobel Prize for chemistry ...