alpha- or beta-thalassemia. In ENERGIZE, results showed a greater percentage of NTD patients treated with mitapivat achieved a hemoglobin response (defined as an increase of at least 1g/dL in ...

Non-transfusion-dependent thalassemia encompasses three clinically distinct forms -- beta-thalassaemia intermedia, hemoglobin E/beta-thalassaemia (mild and moderate forms), and al ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

There are four alpha genes and two beta genes, which means that there’s an immense number of possibilities of different kinds of thalassemias. You most likely have beta thalassemia minor (one ...

There are four alpha genes and two beta genes, which means that there’s an immense number of possibilities of different kinds of thalassemias. You most likely have beta thalassemia minor (one ...

There are four alpha genes and two beta genes, which means that there’s an immense number of possibilities of different kinds of thalassemias. You most likely have beta thalassemia minor (one ...

for the treatment of adult patients with non-transfusion-dependent and transfusion-dependent alpha- or beta-thalassemia, has been accepted for review by the FDA. The supplemental New Drug ...

On January 21st, the Thalassemia International Federation (TIF) and BGI Genomics jointly hosted an educational webinar focused on thalassemia prevention in high-prevalence regions. Experts emphasized ...